



Transforming medicine and changing lives
We are on a never-ending quest to advance genetic technology
and AAV gene therapy
In 1984, one of AskBio’s visionary co-founders asked if a virus could be used to target genetic disease. Researching this question cleared the path for historic advances in genetic medicine, and AskBio is helping to lead the way.

Advancing gene therapy
Treatments for life-altering diseases require new technology to lower the production cost of treatment and increase supply for patients who need it.
Changing lives
Our clinical pipeline is the direct result of listening to patients, their families, their care teams and disease-advocacy organizations.
Putting patient care first
The voices of patients drive everything we do. They propel our research and the urgent need to find treatments.
Work with us
Advancing research
Today’s genetic discoveries are some of the most awe-inspiring advances in medical history. We welcome collaboration with innovative minds in genetic R&D.Building careers
Help transform the face of healthcare with potentially life-changing gene therapy. Every life enriched by our scientific advancements is a result of someone like you.News
First Participant Dosed in AskBio Phase 1/Phase 2 Gene Therapy Trial of AB-1009 for Late-Onset Pompe Disease (LOPD)
AB-1009, an adeno-associated virus (AAV) investigational gene therapy, is being evaluated for the treatment of...
